James Cardia,Michael Byrne,Karen G. Bulock,Pamela A. Pavco,Lyn Libertine
申请号:
US15742093
公开号:
US20180195072A1
申请日:
2016.07.06
申请国别(地区):
US
年份:
2018
代理人:
摘要:
Aspects of the invention relate to methods for treating ALS comprising administering to a subject in need thereof a therapeutically effective amount of a nucleic acid molecule that is directed against a gene encoding superoxide dismutase 1 (SOD1).