Inc.;Ethris GmbH;Shire Human Genetic Therapies;Shire Human Genetic Therapies, Inc.
发明人:
Heartlein, Michael,Guild, Braydon Charles,DeRosa, Frank,Rudolph, Carsten,Plank, Christian
申请号：
AU2018203310
公开号：
AU2018203310A1
申请日:
2018.05.11
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
#$%^&*AU2018203310A120180531.pdf#####ABSTRACT Compositions comprising mRNA formulated for pulmonary administration and related methods for delivery of the mRNA and/or encoded protein to a non-lung cell or tissue. The compositions and methods may be used to prevent or ameliorate the symptoms of diseases associated with the mRNA encoded protein. See Fig. 12.WO 2013/185069 PCT/US2013/044771 12/13 FFL Luminescence in Lung & Liver After Intratracheal Administration of FFL MRT 250000.00 - 6 hr [3 24 hr E3 6 hr 200000.00 0 150000.00 6 0 E 100000.00 E324 hr E6 hr 50000.00 0.00 hr C12-200 C12-200 HGT5001 HGT5001 (Lung) (Liver) (Lung) (Liver) Figure 12
