Methods for treating neurodegenerative diseases using gene therapy to delay disease onset and progression while providing cognitive protection

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专利权人:

University of Iowa Research Foundation

发明人:

Davidson, Beverly L.,Chen, Yong Hong,Tecedor, Luis

申请号：

AU2016341428

公开号：

AU2016341428A1

申请日:

2016.10.24

申请国别(地区):

AU

年份:

2018

代理人:

摘要：

The present disclosure provides methods of treating a lysosomal storage disorder in a mammal which method comprises administering AAV particles encoding a polypeptide directly to the central nervous system of the mammal in conjunction with administering at least two immunosuppressive agents. AAV particles may be delivered by direct injection into the brain, spinal cord, cerebral spinal fluid or a portion thereof.

来源网站：

中国工程科技知识中心

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http://www.ckcest.cn/home/