THE CHILDREN'S MEDICAL CENTER CORPORATION ;PRESIDENT AND FELLOWS OF HARVARD COLLEGE
发明人:
ORKIN Stuart H.,SANKARAN Vijay G.
申请号:
US201815888350
公开号:
US2018179527(A1)
申请日:
2018.02.05
申请国别(地区):
美国
年份:
2018
代理人:
摘要:
The invention relates to methods and uses of modulating fetal hemoglobin expression (HbF) in a hematopoietic progenitor cells via inhibitors of BCL11A expression or activity, such as RNAi and antibodies.