LYSOSOMAL TARGETING OF ENZYMES, AND USES THEREOF

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专利权人:

Shire Human Genetic Therapies; Inc.

发明人:

Bohong ZHANG,Michael F. CONCINO

申请号：

US15521130

公开号：

US20170333569A1

申请日:

2015.10.23

申请国别(地区):

US

年份:

2017

代理人:

摘要：

The invention provides compositions and methods for effective lysosomal targeting mediated by PCSK9. In particular, the compositions and methods provided by the invention may be used to treat lysosomal storage diseases such as Pompe Disease and Sanfilippo Syndrome Type B, and they may be used for targeting lysosomal enzymes to the various muscles of the human body.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/