OPTIONS DE TRAITEMENT DE LA MALADIE DE FABRY
- 专利权人:
- AMICUS THERAPEUTICS, INC.;NATIONAL INSTITUTES OF HEALTH
- 发明人:
- KANESKI, CHRISTINE,SHIN, SANG-HOON,MURRAY, GARY,LUDWIG, KARIN,LOCKHART, DAVID,CASTELLI, JEFF
- 申请号:
- CA2652553
- 公开号:
- CA2652553C
- 申请日:
- 2007.05.16
- 申请国别(地区):
- CA
- 年份:
- 2020
- 代理人:
- 摘要:
- Provided are uses of 1-deoxygalactonojirimycin or a salt for treating Fabrydisease and/orfor enhancing .alpha.-galactosidase A activity.
- 来源网站:
- 中国工程科技知识中心
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