PETIT ARN INTERFERENT (ARNSI) UTILISABLE EN VUE DU TRAITEMENT DE L'OSTEOPOROSE AUTOSOMIQUE DOMINANTE DE TYPE 2 (ADO2) PROVOQUEE PAR UNE MUTATION DU GENE CLCN7 (ADO2 DEPENDANT DE CLCN7)
TETI, ANNA MARIA,RUCCI, NADIA,CAPULLI, MATTIA,MAURIZI, ANTONIO
申请号：
CA2949345
公开号：
CA2949345A1
申请日:
2015.05.21
申请国别(地区):
CA
年份:
2015
代理人:
摘要：
The present invention lies in the field of molecules known as "small interfering RNA" with therapeutic applications. siRNAs have the ability to reduce gene expression in an extremely specific way (1). These are small sequences of double-strand RNA, normally used in laboratory to modify cell function, which revolutionized cell biology by allowing previously precluded molecular manipulations.
