NALDINI, Luigi,ESCOBAR, Giulia,GENTNER, Bernhard Rudolf,MUCCI, Adele
申请号：
SG11201909814W
公开号：
SG11201909814WA
申请日:
2018.04.20
申请国别(地区):
SG
年份:
2019
代理人:
摘要：
INTERNATIONAL APPLICATION PUBLISHED UNDER THE PATENT COOPERATION TREATY (PCT) (19) World Intellectual Property Organization International Bureau (43) International Publication Date 25 October 2018 (25.10.2018) WIPO I PCT oimiolollm °nolo Oil mum olom Env oimIE (10) International Publication Number WO 2018/193119 Al (51) International Patent Classification: C12N 5/0789 (2010.01) A61K 38/21 (2006.01) C12N 5/0786 (2010.01) A61K 39/395 (2006.01) C12N 5/10 (2006.01) A61K 48/00 (2006.01) A61K 31/405 (2006.01) A61P 35/00 (2006.01) A61K 35/15 (2015.01) (21) International Application Number: PCT/EP2018/060238 (22) International Filing Date: 20 April 2018 (20.04.2018) (25) Filing Language: English (26) Publication Language: English (30) Priority Data: 1706410.6 21 April 2017 (21.04.2017) GB 1801511.5 30 January 2018 (30.01.2018) GB (71) Applicants: OSPEDALE SAN RAFFAELE S.R.L. [IT/IT]； Via Olgettina 60, 20132 Milan (IT). FON- DAZIONE TELETHON [IT/IT]； Via Varese 16B, 00185 Rome (IT). (72) Inventors: NALDINI, Luigi； San Raffaele Telethon Insti- tute for Gene Therapy (TIGET), Via Olgettina 58, 20132 Milan (IT). ESCOBAR, Giulia； San Raffaele Telethon In- stitute for Gene Therapy (TIGET), Via Olgettina 58, 20132 Milan (IT). GENTNER, Bernhard Rudolf； San Raffaele Telethon Institute for Gene Therapy (TIGET), Via Olget- tina 58, 20132 Milan (IT). MUCCI, Adele； San Raffaele Telethon Institute for Gene Therapy (TIGET), Via Olgetti- na 58, 20132 Milan (IT). (74) Agent: D YOUNG & CO LLP； 120 Holborn, London EC1N 2DY (GB). (81) Designated States (unless otherwise indicated, for every kind of national protection available): AE, AG, AL, AM, AO, AT, AU, AZ, BA, BB, BG, BH, BN, BR, BW, BY, BZ, CA, CH, CL, CN, CO, CR, CU, CZ, DE, DJ, DK, DM, DO, DZ, EC, EE, EG, ES, FI, GB, GD, GE, GH, GM, GT, HN, HR, HU, ID, IL, IN, IR, IS, JO, JP, KE, KG, KH, KN, KP, KR, KW, KZ, LA, LC, LK, LR, LS, LU, LY, MA, MD, ME, MG, MK, MN, MW, MX, MY, MZ, NA, NG, NI, NO, NZ, OM, PA, PE, PG, PH, PL, PT, QA, RO, RS, RU,
