Research Institute at Nationwide Children's Hospital;Research Institute at Nationwide Childrens Hospital
发明人:
Rodino-Klapac, Louise,Mendell, Jerry R.
申请号：
AU2017250791
公开号：
AU2017250791A1
申请日:
2017.04.14
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
The invention provides for recombinant AAV vectors comprising a miniaturized human micro-dystrophin gene and methods of using the recombinant vectors to reduce or prevent fibrosis in subjects suffering from muscular dystrophy.
