GENE THERAPY CONSTRUCTS AND METHODS OF USE
- 专利权人:
- Inc.;Amicus Therapeutics
- 发明人:
- Hung DO,Steven TUSKE,Russell GOTSCHALL,Ce Feng LIU
- 申请号:
- US16399979
- 公开号:
- US20190343968A1
- 申请日:
- 2019.04.30
- 申请国别(地区):
- US
- 年份:
- 2019
- 代理人:
- 摘要:
- Provided herein are improved gene therapy vectors and methods of use, in some embodiments, comprising sequences for improved expression and cellular targeting of a therapeutic protein.
- 来源网站:
- 中国工程科技知识中心