GREEN, MICHAEL R.,FANG, MINGGANG,KOWTONIUK, WALTER
申请号:
CA2998745
公开号:
CA2998745A1
申请日:
2016.09.16
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
The disclosure relates to methods and compositions for reactivating a silenced FMR1 gene. In some aspects, methods described by the disclosure are useful for treating a FMR1- inactivation-associated disorder (e.g., fragile X syndrome).