Baylor College of Medicine; Inc.;Ionis Pharmaceuticals, Inc.;Ionis Pharmaceuticals
发明人:
ZOGHBI, Huda, Y.,SZTAINBERG, Ezequiel,FREIER, Susan, M.
申请号：
EP16759471
公开号：
EP3265564A4
申请日:
2016.03.03
申请国别(地区):
EP
年份:
2018
代理人:
摘要：
Disclosed herein are methods for decreasing MECP2 mRNA and protein expression. Such methods are useful to treat, prevent, or ameliorate MECP2 associated disorders and syndromes. Such MECP2 associated disorders include MECP2 duplication syndrome.
