Delivery of mrna for the augmentation of proteins and enzymes in human genetic diseases

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专利权人:

Shire Human Genetic Therapies

发明人:

Heartlein Michael,Derosa Frank,Concino Michael,Guild Braydon Charles

申请号：

NZ71619210

公开号：

NZ716192A

申请日:

2010.11.30

申请国别(地区):

NZ

年份:

2017

代理人:

摘要：

Disclosed is the cationic lipid, Imidazole Cholesterol Ester (ICE), and methods of preparing said lipid, in a composition for modulating the expression of a protein in a target cell

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/