THE MEDICAL COLLEGE OF WISCONSIN, INC;UNIVERSITY HEALTH NETWORK;WASHINGTON UNIVERSITY IN ST. LOUIS
发明人:
Jeffrey A. Medin,John F. Dipersio,Murtaza S. Nagree
申请号:
US16619883
公开号:
US20200181582A1
申请日:
2018.06.06
申请国别(地区):
US
年份:
2020
代理人:
摘要:
The present invention is related to a dual promoter lentiviral vector and methods of use for the treatment of diseases and disorders, specifically lysosomal storage disorders.