Alfica Sehgal,Alla A. Sigova,Igor Zlobine,Brian E. Schwartz,David A. Bumcrot
申请号:
US16753530
公开号:
US20200316038A1
申请日:
2018.10.09
申请国别(地区):
US
年份:
2020
代理人:
摘要:
The present invention provides methods and compositions for the treating a patient with a urea cycle disorder. Methods and compositions are also provided for modulating genes encoding enzymes that participate in the urea cycle by altering gene signaling networks.