WILSON, JAMES M.,SIDRANE, JENNY AGNES,GOVINDASAMY, LAKSHMANAN
申请号：
CA3048044
公开号：
CA3048044A1
申请日:
2017.12.29
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
Compositions and regimens useful in treating Wilson's Disease are provided. The compositions include recombinant adeno-associated virus (rAAV) with a transthyretin enhancer and promoter driving expression of a human ATP7B.
