Nina N. Raben,Cynthia Schreiner,Rebecca Baum,Shoichi Takikita,Tao Xie,Paul H. Plotz
申请号：
US13391265
公开号：
US08536148B2
申请日:
2010.09.02
申请国别(地区):
US
年份:
2013
代理人:
摘要：
Provided herein are methods of treating lysosomal storage disease, for instance Pompe disease, through inhibition of autophagy. Optionally, treatment is administered as an adjunct to enzyme replacement therapy (ERT).
