KAKKIS, EMIL,VELLARD, MICHEL CLAUDE,SWISTOWSKI, ANDRZEJ
申请号:
CA3002410
公开号:
CA3002410A1
申请日:
2016.10.28
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
Methods and compositions for the treatment or prevention of amyloidosis are provided. In some embodiments, the methods comprise administering to the subject a therapeutically effective amount of at least one catabolic enzyme or a biologically active fragment thereof. Such methods and compositions may be employed reduce, prevent, degrade and/or eliminate amyloid formation in the lysosome and/or extracellularly.