Suhy, David,Graham, Michael,Trollet, Capucine,Malerba, Alberto,Dickson, George J.
申请号：
AU2017250017
公开号：
AU2017250017A1
申请日:
2017.04.13
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
The present disclosure relates to RNA interference (RNAi) reagents targeting PABPN1 for treatment of oculopharyngeal muscular dystrophy (OPMD), compositions comprising same, and use thereof to treat individuals suffering from OPMD or which are predisposed thereto.
