National Center of Neurology and Psychiatry;Nippon Shinyaku Co., Ltd.
发明人:
申请号:
EP19188572.2
公开号:
EP3581655A1
申请日:
2011.08.31
申请国别(地区):
EP
年份:
2019
代理人:
摘要:
The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency.The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.