rectal phenylbutyrate for the treatment of motor neuronal disease, a urea cycle disorder or cancer

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专利权人:

GMP - ORPHAN

发明人:

FRÉDÉRIC MARINI

申请号：

BR112013033192

公开号：

BR112013033192A2

申请日:

2012.06.22

申请国别(地区):

BR

年份:

2017

代理人:

摘要：

The present invention relates to rectal administration of phenylbutyrate for treating a motor neuron disease, such as, for example, spinal muscular atrophy or a metabolic disease such as, for example, an urea cycle disorder, related methods and compositions.

来源网站：

中国工程科技知识中心

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http://www.ckcest.cn/home/