COMPOSIÇÕES DE SKIPPING DE EXÕES PARA O TRATAMENTO DA DISTROFIA MUSCULAR
- 专利权人:
- SAREPTA THERAPEUTICS; INC.
- 发明人:
- RICHARD K. BESTWICK,DIANE ELIZABETH FRANK
- 申请号：
- PT14723583
- 公开号：
- PT2970964T
- 申请日:
- 2014.03.14
- 申请国别(地区):
- PT
- 年份:
- 2019
- 代理人:
- 摘要：
- Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.
- 来源网站：
- 中国工程科技知识中心
