OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA

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专利权人:

SAREPTA THERAPEUTICS; INC.

发明人:

KOLE, RYSZARD,BESTWICK, RICHARD, KEITH

申请号：

RSP20180774

公开号：

RS57467B1

申请日:

2012.12.07

申请国别(地区):

RS

年份:

2018

代理人:

摘要：

Provided are methods of treatment in subjects having progeroid diseases and related conditions which rely upon LMNA-targeted antisense oligonucleotides for reducing expression of one or more aberrantly spliced LMNA mRNA isoforms that encode progerin.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/