GABRIEL MARTINEZ BOTELLA,JAMES J. DOHERTY,MICHAEL C. QUIRK
申请号:
BR112017007053
公开号:
BR112017007053A2
申请日:
2015.10.07
申请国别(地区):
BR
年份:
2018
代理人:
摘要:
Methods for treating a subject suffering from a sterol synthesis disorder or a sterol deficiency disorder, e.g., Smith-Lemli-Opitz syndrome, the method comprising administering to the subject an effective amount of an NMDA receptor modulating compound, are provided.