COMPOSITIONS AND METHODS FOR TREATING PHENYLKETONURIA

• 收藏
• 分享

专利权人:

American Gene Technologies International Inc.

发明人:

Tyler Lahusen,Charles David Pauza

申请号：

US16494196

公开号：

US20200087682A1

申请日:

2018.04.02

申请国别(地区):

US

年份:

2020

代理人:

摘要：

A lentiviral vector system for expressing a lentiviral particle is disclosed. The lentiviral vector system includes a therapeutic vector. The therapeutic vector comprises a phenylalanine hydroxylase (PAH) sequence for expressing at least one of PAH or a variant thereof, wherein the PAH sequence is truncated.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/